Risdiplam-Treated Infants with Type 1 Spinal Muscular Atrophy versus Historical Controls (2021)
- Authors:
- Autor USP: ZANOTELI, EDMAR - FM
- Unidade: FM
- DOI: 10.1056/NEJMoa2102047
- Subjects: ATROFIA MUSCULAR; MEDULA ESPINHAL; LACTENTES; COMPOSTOS ORGÂNICOS; COMPOSTOS HETEROCÍCLICOS; ÍNDICE DE GRAVIDADE DA DOENÇA
- Language: Inglês
- Imprenta:
- Source:
- Título do periódico: New england journal of medicine
- ISSN: 0028-4793
- Volume/Número/Paginação/Ano: v. 385, n. 5, p. 427-435, 2021
- Este periódico é de assinatura
- Este artigo é de acesso aberto
- URL de acesso aberto
- Cor do Acesso Aberto: bronze
-
ABNT
DARRAS, Basil T. et al. Risdiplam-Treated Infants with Type 1 Spinal Muscular Atrophy versus Historical Controls. New england journal of medicine, v. 385, n. 5, p. 427-435, 2021Tradução . . Disponível em: https://doi.org/10.1056/NEJMoa2102047. Acesso em: 02 jun. 2024. -
APA
Darras, B. T., Masson, R., Mazurkiewicz-beldzinska, M., Rose, K., Xiong, H., Zanoteli, E., et al. (2021). Risdiplam-Treated Infants with Type 1 Spinal Muscular Atrophy versus Historical Controls. New england journal of medicine, 385( 5), 427-435. doi:10.1056/NEJMoa2102047 -
NLM
Darras BT, Masson R, Mazurkiewicz-beldzinska M, Rose K, Xiong H, Zanoteli E, Baranello G, Bruno C, Vlodavets D, Wang Y. Risdiplam-Treated Infants with Type 1 Spinal Muscular Atrophy versus Historical Controls [Internet]. New england journal of medicine. 2021 ; 385( 5): 427-435.[citado 2024 jun. 02 ] Available from: https://doi.org/10.1056/NEJMoa2102047 -
Vancouver
Darras BT, Masson R, Mazurkiewicz-beldzinska M, Rose K, Xiong H, Zanoteli E, Baranello G, Bruno C, Vlodavets D, Wang Y. Risdiplam-Treated Infants with Type 1 Spinal Muscular Atrophy versus Historical Controls [Internet]. New england journal of medicine. 2021 ; 385( 5): 427-435.[citado 2024 jun. 02 ] Available from: https://doi.org/10.1056/NEJMoa2102047 - Myopathy due to HMGCR antibodies in adult mimicking muscular dystrophy associated with cancer and statin exposure - narrative review of the literature - case report
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Informações sobre o DOI: 10.1056/NEJMoa2102047 (Fonte: oaDOI API)
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